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In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model. https://www.padiracinnovation.org/News/2022/12/in-vivo-genome-editing-using-novel-aav-php-variants-rescues-motor-function-deficits-and-extends-survi
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In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model. https://www.padiracinnovation.org/News/2022/12/in-vivo-genome-editing-using-novel-aav-php-variants-rescues-motor-function-deficits-and-extends-survi
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