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Muscle-specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1 https://journal.hep.com.cn/ctm/EN/10.1002/ctm2.70227
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Muscle-specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1 https://journal.hep.com.cn/ctm/EN/10.1002/ctm2.70227
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